Procysbi Approved for NHS Scotland in Rare Kidney Disease
The Scottish Medicines Consortium has approved Procysbi for use in NHS Scotland to treat nephropathic cystinosis, a rare kidney disorder that strikes young children. This decision on November 10, 2025, brings new hope to families by offering a more convenient treatment option that could ease daily struggles. Understanding Nephropathic Cystinosis Nephropathic cystinosis is a genetic condition that causes cystine, an amino acid, to build up in the body's cells. This buildup damages organs, especially the kidneys, and often leads to kidney failure by age 10 if left untreated. Doctors diagnose it in infants through symptoms like excessive thirst, frequent urination,…
